HMX Pro Genetics: Nucleic Acid Therapeutics

Harvard HMS

Even with the thousands of approved small molecule drugs at our disposal, there remains a lack of effective prevention and treatment for many diseases. Fortunately, a new and exciting drug modality has emerged called nucleic acid therapeutics that has the potential to address current unmet needs.This class of drugs uses nucleic acids and closely related compounds for a variety of applications, including regulating gene expression, stimulating the immune system, editing the genome, or…