HMX Pro Genetics: Gene Therapy

Harvard HMS

In recent years, close collaboration between multiple scientific disciplines has rendered gene therapy a viable treatment option for some genetic conditions, and a promising pursuit for many others. As of today, there are numerous clinical trials underway for gene therapy treatments of various cancers, blood disorders, neurological diseases, and inherited retinal disorders to name a few. Advancements in vector science, gene editing technologies, and our understanding of the molecular…